We are delighted to announce the selection of the c4c consortium’s first portfolio of pan-European paediatric studies aimed at advancing the understanding of high priority medicines commonly used in babies, children and young people in Europe. The four inaugural studies will be conducted by academic institutions, in addition to three or four studies by industry partners, covering different diseases and age groups. The selected studies will implement new ways to: • Ensure that the experiences and preferences of children and young people are reflected in clinical trial design and minimise the burden […]
The countdown has begun to Rare Disease Day 2019 on 28th February. People around the world are joining the global movement for rare diseases by taking part in the #ShowYourRare campaign, holding events and raising awareness. This year’s theme is ‘Bridging health and social care’, and it is an opportunity to be part of a global call on policy makers, healthcare professionals, and care services to better coordinate all aspects of care for rare disease patients and families.